Imagine switching brain circuits on and off using only magnetic fields. Researchers have just developed a cutting-edge gene therapy that...

A team from the Broad Institute of MIT and Harvard, along with Harvard University and the Howard Hughes Medical Institute, has made...

The fight against diabetes is being revolutionized with an innovative approach from Genprex, with its gene therapy candidate, GPX-002....

On August 2nd, 2024, the FDA granted accelerated approval for afami-cel -- the first gene-engineered T-cell Therapy for advanced...

In a project funded by the National Institute of Mental Health (NIMH) and the National Institute of Neurological Disorders and Stroke...

Gene Therapy Using AAV9 Reverses Brain Abnormalities in FOXG1 Syndrome in Infant Mice In a major breakthrough for gene therapy,...

On June 20th, 2024, the FDA expanded its approval of ELEVIDYS , an innovative AAV-based gene therapy developed by Sarepta Therapeutics ,...

Gene therapy is transforming the landscape of treatment options, and the recent FDA approval of BEQVEZ marks a significant milestone for...

In a promising study, scientists from the Mayo Clinic and Yale University utilized brain organoids —tiny brain models grown from human...

Lenmeldy , a groundbreaking gene therapy developed by Orchard Therapeutics , has recently received FDA approval , making it the first and...

The AK-OTOF-101 clinical trial by Akouos, Inc., a subsidiary of Lilly & Co., brings renewed hope to children suffering from congenital...

The FDA recently approved two groundbreaking CRISPR-based gene therapies for curing Sickle Cell Disease (SCD): Casgevy  - developed by...

Penn Medicine research offers promising insights into AAV-based gene therapies' safety: Integration into human DNA is unlikely to trigger...

New Approach for Liver Cancer Treatment and Possible Prevention: Gene Therapy Targets Biomarker for Hepatocellular Carcinoma (HCC)...